Pérez-Maroto, J.Sepp-Lorenzino, L.Castaño-Esteban, D.Palacios, D.Sot, Begoña2026-03-042026-03-042025https://hdl.handle.net/20.500.12614/4238enAdvancements in Nonviral Gene Editing Strategies for Rare Diseasesresearch article10.1177/10430342251372056