Publication: Advancements in Nonviral Gene Editing Strategies for Rare Diseases
| dc.contributor.affiliation | 000000041762408X | |
| dc.contributor.affiliation | Biomedical Innovation Unit, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Madrid, Spain; Advanced Therapies Unit, Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, Madrid, Spain; Intellia Therapeutics, Inc., Cambridge, United States; Consiglio Nazionale delle Ricerche, Rome, Italy; IMDEA Nanociencia, Madrid, Spain | en |
| dc.contributor.author | Pérez-Maroto, J. | |
| dc.contributor.author | Sepp-Lorenzino, L. | |
| dc.contributor.author | Castaño-Esteban, D. | |
| dc.contributor.author | Palacios, D. | |
| dc.contributor.author | Sot, Begoña | |
| dc.date.accessioned | 2026-03-04T12:51:30Z | |
| dc.date.available | 2026-03-04T12:51:30Z | |
| dc.date.issued | 2025 | |
| dc.identifier.doi | 10.1177/10430342251372056 | en |
| dc.identifier.uri | https://hdl.handle.net/20.500.12614/4238 | |
| dc.issue.number | Atribución-NoComercial-SinDerivadas 3.0 España | en |
| dc.journal.title | Human Gene Therapy | en |
| dc.language.iso | en | en |
| dc.page.initial | open access | en |
| dc.relation.projectIDTEMP | This work was supported by the Ministerio de Ciencia, Innovaci\u00F3n y Universidades, Spain (PID2023-146982OB-I00). | |
| dc.title | Advancements in Nonviral Gene Editing Strategies for Rare Diseases | en |
| dc.type | research article | en |
| dc.volume.number | http://creativecommons.org/licenses/by-nc-nd/3.0/es/ | en |
| dspace.entity.type | Publication | |
| relation.isAuthorOfPublication | eba25d11-41ca-4b82-9b2d-9798e6bdcef8 | |
| relation.isAuthorOfPublication.latestForDiscovery | eba25d11-41ca-4b82-9b2d-9798e6bdcef8 |

