Publication:
Advancements in Nonviral Gene Editing Strategies for Rare Diseases

dc.contributor.affiliation000000041762408X
dc.contributor.affiliationBiomedical Innovation Unit, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Madrid, Spain; Advanced Therapies Unit, Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, Madrid, Spain; Intellia Therapeutics, Inc., Cambridge, United States; Consiglio Nazionale delle Ricerche, Rome, Italy; IMDEA Nanociencia, Madrid, Spainen
dc.contributor.authorPérez-Maroto, J.
dc.contributor.authorSepp-Lorenzino, L.
dc.contributor.authorCastaño-Esteban, D.
dc.contributor.authorPalacios, D.
dc.contributor.authorSot, Begoña
dc.date.accessioned2026-03-04T12:51:30Z
dc.date.available2026-03-04T12:51:30Z
dc.date.issued2025
dc.identifier.doi10.1177/10430342251372056en
dc.identifier.urihttps://hdl.handle.net/20.500.12614/4238
dc.issue.numberAtribución-NoComercial-SinDerivadas 3.0 Españaen
dc.journal.titleHuman Gene Therapyen
dc.language.isoenen
dc.page.initialopen accessen
dc.relation.projectIDTEMPThis work was supported by the Ministerio de Ciencia, Innovaci\u00F3n y Universidades, Spain (PID2023-146982OB-I00).
dc.titleAdvancements in Nonviral Gene Editing Strategies for Rare Diseasesen
dc.typeresearch articleen
dc.volume.numberhttp://creativecommons.org/licenses/by-nc-nd/3.0/es/en
dspace.entity.typePublication
relation.isAuthorOfPublicationeba25d11-41ca-4b82-9b2d-9798e6bdcef8
relation.isAuthorOfPublication.latestForDiscoveryeba25d11-41ca-4b82-9b2d-9798e6bdcef8

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